2025 World Orphan Drug Congress: “Developing a Checklist for Patient Engagement in Rare Disease Value Research”
2025 NORD Breakthough Summit: “Co-Creating Guidance and a Checklist for Rare Disease Value Research through Meaningful Patient and Caregiver Engagement”
Engaging Patients with Rare Disease in Identifying Meaningful Approaches to integrate Patient-Centered Outcomes inComparative Effectiveness Research and Value Assessment
