The RDPE Guidance & Checklist is designed for mixed teams involved in rare disease evidence generation and decision-making, including:

  • Researchers and methodologists working on CER, economic models, and other value studies.
  • Patient and caregiver partners and advocacy organizations collaborating on research and assessment projects.
  • HTA bodies and payers reviewing evidence and making coverage and benefit design decisions.
  • Clinicians and clinical researchers who help design and implement studies with people living with rare diseases.